The success of gene therapy relies on the safe and efficient delivery of genetic material into affected cells using a suitable vector. Several gene and cell therapy products have already received approval from the US Food and Drug Administration to treat various indications including neuromuscular conditions, inherited forms of blindness and certain blood cancers.
Innovations in gene therapy technologies can significantly expand the impact of these cutting-edge therapeutics.
Download this listicle to explore recent advances in gene therapy such as:
- Novel virus-free delivery systems
- Precision targeting using lipid nanoparticles
- Safer gene editing systems